A potential next-generation therapy, golodirsen (SRP-4053) facilitates and increases dystrophin production in Duchenne muscular dystrophy (DMD) patients, an interim analysis of a Phase 1/2 trial being presented at the 2018 American Academy of Neurology (AAN) Annual Meeting in Los Angeles reports. These findings, in “Golodirsen Induces Exon Skipping Leading to Sarcolemmal Dystrophin Expression in Duchenne Muscular Dystrophy Patients With Mutations […]
How far would you go for someone you love?
That’s the question that led to the birth of Jesse’s Journey when one family dared to dream about what’s possible after learning the crushing news that Duchenne muscular dystrophy had become a part of their daily lives.
When John and Sherene Davidson learned that their middle son Jesse was diagnosed with Duchenne they charted a life changing course for themselves-setting out to raise research funds to find the elusive cure.