The U.S. Food and Drug Administration has placed a clinical hold on a Phase 1/2 trial testing SGT-001, a dystrophin gene therapy intended to treat Duchenne muscular dystrophy (DMD), after the first patient dosed was hospitalized with a possibly serious reaction. Solid Biosciences, the therapy’s developer, announced that within days of being given SGT-001 at 5E13 vg/kg […]
How far would you go for someone you love?
That’s the question that led to the birth of Jesse’s Journey when one family dared to dream about what’s possible after learning the crushing news that Duchenne muscular dystrophy had become a part of their daily lives.
When John and Sherene Davidson learned that their middle son Jesse was diagnosed with Duchenne they charted a life changing course for themselves-setting out to raise research funds to find the elusive cure.