Jesse's Journey Foundation

Defeat Duchenne. Change Lives.

Defeat Duchenne Family Forum and Celebration Dinner

Presented by:

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The first-ever Defeat Duchenne Family Forum and Celebration Dinner (Saturday, May 25 in London, Ontario)

This unique event – tailored to families in Canada affected by Duchenne muscular dystrophy – featured updates about the latest research, clinical trials recruiting in Canada, and more.

Introduction to Effective Advocacy: Advocacy Solutions

Dr. Craig Campbell: Standards of care in Duchenne

Researcher Panel: Dr. Craig Campbell, Dr. Jerry Mendell, Dr. Evgueni (Zhenya) Ivakine

Dr. Jerry Mendell

Brett Billmeyer: PTC Therapeutics - Measured by Moments

Treatment Preferences for Duchenne muscular dystrophy community

Gene Therapy 2.0: Interrogation of genome editing applications for the treatment of DMD

Advocacy Hub

Maria Mancini – Vice President, Clinical Operations, Catabasis Pharmaceuticals

Slide Deck Topic: PolarisDMD: A Phase 3 Clinical Trial of Edasalonexent in Duchenne Enrolling Patients Globally

Mancini, Maria – Catabasis

Learn more about our Speakers (click on the speaker’s name for session description and bio)

Dr. Craig Campbell – Pediatric Neurologist , Children’s Hospital – London Health Sciences Centre

Dr. Jerry Mendell – Founder of the Clinical Translational Gene Therapy Program at the Research Institute at Nationwide Children’s Hospital
Topic: DMD Gene Therapy Clinical Trial: Making a difference by gene replacement

Dr. Evgueni (Zhenya) Ivakine – Lab Director, Cohn Lab – Sick Kids Hospital
Topic: Gene therapy 2.0: Interrogation of genome editing applications for the treatment of Duchenne muscular dystrophy

Norah (Nonie) Crossnohere – Research Associate, Ohio State University Wexner Medical Center, PhD candidate – Johns Hopkins Bloomberg School of Public Health
Topic: Treatment preferences for Duchenne muscular dystrophy community: An international study

Maria Mancini – Vice President, Clinical Operations, Catabasis Pharmaceuticals
Topic: PolarisDMD: A Phase 3 Clinical Trial of Edasalonexent in Duchenne Enrolling Patients Globally 

Ryan Clarke and Joanne Koskie – Advocacy Solutions
Topic: Introduction to Effective Advocacy: Learn How to Be Heard

Brett Billmeyer – Patient Engagement, PTC Therapeutics
Topic: PTC Therapeutics – Measured by Moments

Sponsored by:

Catabasis Pharmaceuticals

Westminster College Foundation

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