May 12, 2020
Due to COVID-19, the Defeat Duchenne Family Forum presented by PTC Therapeutics and in partnership with La Force DMD has been transformed from a one-day “in-person” program into a series of four virtual events taking place May 20 – 30, 2020. Join us as families and caregivers navigating the Duchenne journey across Canada come together with researchers, clinicians, and […]
May 12, 2020
The Walk to Defeat Duchenne presented by Sbenati Dentistry has been rescheduled to Monday, September 7, 2020 (World Duchenne Awareness Day) – this means more time to grow your team and raise vital funds! While making plans during this uncertain time is challenging, we hope you will refocus your efforts online – by encouraging your supporters to […]
April 28, 2020
Italfarmaco has provided an update regarding the Givinostat clinical trial for the Duchenne community: The Interim data from EPYDIS Phase 3 trial shows that the trial is not futile and the Independent Data Monitoring Committee recommends trial continuation. Blinded re-estimation of the study sample size allows a reduction of the total number of subjects to […]
March 30, 2020
Catabasis has shared its March 2020 update: Catabasis provided an update regarding COVID-19 and Duchenne, FAQ’s, and shared the presentation slides from the MDA Virtual Clinical Trials Session. March 2020 – Catabasis Connection Issue 25 Edasalonexent Update: In Duchenne, the loss of dystrophin leads to chronic activation of NF-kB, which is a key driver of […]
March 24, 2020
Santhera Pharmaceuticals shared its 2019 Annual Results and Highlights Piepleine Progress for Duchenne muscular dystrophy. “Santhera is emerging as a leader in addressing rare neuromuscular diseases and 2019 saw us prepare the business for several significant value inflection points this year for our drug candidatesto treat DMD,” said Dario Eklund, CEO of Santhera. “The regulatory […]
March 12, 2020
Solid Biosciences Inc. has provided an update on the IGNITE DMD phase I/II microdystrophin gene therapy clinical program. As previously reported in late 2019, the IGNITE DMD clinical program was placed on hold. Today, they announced the biomarker data from the third patient dosed in the 2E14 vg/kg dose cohort of IGNITE DMD, including three-month […]
February 28, 2020
Catabasis has shared its February 2020 update: “February is all about the heart and that’s a big focus for us, too! Because the cardiac function is so vital to those affected by Duchenne, we’re passionate to learn more about the heart and edasalonexent in our Phase 3 PolarisDMD trial. In young boys affected by Duchenne, […]
February 27, 2020
Did you know approximately 1 in 12 Canadians, two-thirds of them children, are affected by a rare disease? Saturday, February 29, 2020, is Rare Disease Day, and we ask for your help in raising awareness of Duchenne muscular dystrophy. Though Duchenne is the most common fatal genetic disorder diagnosed in childhood, it is considered a […]
February 3, 2020
Jesse’s Journey is proud to represent the Duchenne community in the new neuromuscular network for Canada, NMD4C (NMD for Canada). The neuromuscular network for Canada brings together the country’s leading clinical, scientific, technical and patient expertise to improve care, research and collaboration in neuromuscular disease. Launched in January 2020 with funding from the Canadian Institutes of Health […]
January 28, 2020
2020 is an exciting year for Jesse’s Journey as we celebrate our past and ignite a bold new vision for our future. This year marks the 25th anniversary of the organization as our founder, John Davidson, set out on an incredible mission to push his son, Jesse, across Ontario in his wheelchair – a trek of 3,339 […]
