February 3, 2020
Jesse’s Journey is proud to represent the Duchenne community in the new neuromuscular network for Canada, NMD4C (NMD for Canada). The neuromuscular network for Canada brings together the country’s leading clinical, scientific, technical and patient expertise to improve care, research and collaboration in neuromuscular disease. Launched in January 2020 with funding from the Canadian Institutes of Health […]
January 28, 2020
2020 is an exciting year for Jesse’s Journey as we celebrate our past and ignite a bold new vision for our future. This year marks the 25th anniversary of the organization as our founder, John Davidson, set out on an incredible mission to push his son, Jesse, across Ontario in his wheelchair – a trek of 3,339 […]
January 22, 2020
Santhera Pharmaceuticals have shared their January update. “Our main focus in the U.S. in the first half of the year is to bring the SIDEROS clinical trial to full enrollment and we ask the community’s help, now more than ever, to achieve this goal. The SIDEROS clinical trial, which investigates the safety and efficacy […]
December 24, 2019
Sarepta Therapeutics Announces Partnership with Roche in Territories Outside the United States for its Investigational Micro-dystrophin Gene Therapy for Duchenne Muscular Dystrophy, SRP-9001 “…Sarepta and Roche have entered into a licensing agreement that would provide Roche exclusive rights to SRP-9001 (AAVrh74.MHCK7.micro-dystrophin) outside of the United States. As a mission-driven organization committed to families impacted by […]
November 29, 2019
Jesse’s Journey is proud to announce its gift of $300,000 towards a breakthrough clinical trial, which may empower local researchers to discover a therapeutic solution to the degenerative disease Duchenne muscular dystrophy. The clinical trial is building upon promising Phase I research involving myoblast transplantation. This therapeutic approach applies to all Duchenne patients, independently of […]
November 12, 2019
More than 75 Canadians came together for the inaugural Defeat Duchenne Family Forum presented by PTC Therapeutics on Saturday, November 2, 2019, in Calgary, Alberta. Families from across Western Canada affected by Duchenne muscular dystrophy came together with world-renowned researchers, clinicians, and industry professionals for a day of education, inspiration, and hope. Read more here.
November 12, 2019
Unless you’ve experienced it for yourself, it’s nearly impossible to understand the ramifications of finding out your loved one has Duchenne muscular dystrophy. Jesse’s Journey is lucky to have the support of families who are brave enough to share their stories because they know it’s the only way we can hope to inspire understanding and […]
October 24, 2019
from Joana Carvalho, MSc
Vamorolone, an experimental treatment for Duchenne muscular dystrophy (DMD) being developed by ReveraGen Biopharma, continues to improve muscle function in DMD patients with fewer side effects than standard corticosteroids, topline data in 23 boys in an ongoing Phase 2 trial show. These findings were detailed in a late-breaking presentation by Eric Hoffman, PhD, chief executive […]
October 21, 2019
from Matt Hoffman
Phase 2 study results of edasalonexent, an investigational oral small molecule NF-kB inhibitor for the treatment of Duchenne muscular dystrophy (DMD), suggest that the therapy is associated with slowed disease progression, as well as a good safety profile over the course of more than 50 patient-years of exposure in boys with the disease.1 Treatment with […]
May 28, 2019
With over 7,000 rare conditions already identified and dozens more being discovered every day, it is estimated that rare diseases impact 1 in 12 Canadians, two-thirds of whom are children. But each disease affects only a handful of individuals, so understanding and medical expertise are limited and uneven across the country. Many of these conditions […]
